Last Monday was another landmark day for gene therapies as a new and potentially curative one-off gene therapy for babies with spinal muscular atrophy (SMA) looks set to become the most expensive treatment ever recommended by NICE.
Share this post
Lessons from recent EU payer decisions on…
Share this post
Last Monday was another landmark day for gene therapies as a new and potentially curative one-off gene therapy for babies with spinal muscular atrophy (SMA) looks set to become the most expensive treatment ever recommended by NICE.